Poster

Translation of an AAV-Delivered Gene Editing Approach for Transthyretin Amyloidosis in Animal Models

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Greig, J.A. et al. American Society of Gene and Cell Therapy (ASGCT) 2021 Annual Meeting.

A Gene Editing Approach to Eliminate Hepatitis B Virus Using ARCUS Meganucleases

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Gorsuch, C. et al. American Society of Gene and Cell Therapy (ASGCT) 2020 Annual Meeting.

Engineering a Self-inactivating Adeno-associated Virus (AAV) Vector for ARCUS Nuclease Delivery

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Li, H. et al. American Society of Gene and Cell Therapy (ASGCT) 2020 Annual Meeting.

ARCUS gene editing of Apolipoprotein C3 results in substantial reduction in serum triglycerides in vivo

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Shoop W., et al. European Society of Gene & Cell Therapy (ESGCT) 2022 Annual Congress.

ARCUS Gene Editing to Eliminate MELAS-Associated m.3243A>G Mutant Mitochondrial DNA

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Shoop W., et al. American Society of Gene and Cell Therapy (ASGCT) 2022 Annual Meeting.

Development of a Clinical-Grade Meganuclease for Allogeneic CAR T Cell Production​

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Lape, J. et al. American Society of Gene and Cell Therapy (ASGCT) 2018 Annual Meeting.

Allogeneic CAR T cells with Deoxycytidine Kinase Knockdown Demonstrate Resistance to Fludarabine

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Pires, M. et al. Journal for ImmunoTherapy of Cancer. 9,6 (2021). Society for Immunotherapy of Cancer (SITC) 2021 Annual Meeting.

Initial Findings of the Phase 1 Trial of PBCAR0191, a CD19 Targeted Allogeneic CAR T Cell Therapy

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Jacobson C.A. et al. American Society of Hematology (ASH) 2019 Annual Meeting.