Poster

Translation of an AAV-Delivered Gene Editing Approach for Transthyretin Amyloidosis in Animal Models

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Greig, J.A. et al. American Society of Gene and Cell Therapy (ASGCT) 2021 Annual Meeting.

Unique features of ARCUS nucleases enable high efficiency, targeted gene insertion in vivo

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Gorsuch, C., et al. European Society of Gene and Cell Therapy (ESGCT) 2023 Annual Congress.

Preclinical efficacy and safety of ARCUS-POL nucleases for chronic hepatitis B: a potentially curative strategy

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Harrison E., et al. American Association for the Study of Liver Diseases (AASLD) The Liver Meeting 2023.

ARCUS gene editing of Apolipoprotein C3 results in substantial reduction in serum triglycerides in vivo

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Shoop W., et al. European Society of Gene & Cell Therapy (ESGCT) 2022 Annual Congress.

ARCUS Gene Editing to Eliminate MELAS-Associated m.3243A>G Mutant Mitochondrial DNA

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Shoop W., et al. American Society of Gene and Cell Therapy (ASGCT) 2022 Annual Meeting.

Development of a Clinical-Grade Meganuclease for Allogeneic CAR T Cell Production​

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Lape, J. et al. American Society of Gene and Cell Therapy (ASGCT) 2018 Annual Meeting.

Allogeneic CAR T cells with Deoxycytidine Kinase Knockdown Demonstrate Resistance to Fludarabine

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Pires, M. et al. Journal for ImmunoTherapy of Cancer. 9,6 (2021). Society for Immunotherapy of Cancer (SITC) 2021 Annual Meeting.