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Mitochondrial Targeted Meganuclease as a Platform to Eliminate Mutant mtDNA In Vivo
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Long-Term Stable Reduction of Low-Density Lipoprotein in Nonhuman Primates Following In Vivo Genome Editing of PCSK9
Wang, L. et al. Molecular Therapy. 6, 2019-2029 (2021).
Meganuclease targeting of PCSK9 in macaque liver leads to stable reduction in serum cholesterol
Wang, L. et al. Nat Biotechnol. 8, 717-725 (2018).
Integration of a CD19 CAR Into the TCR Alpha Chain Locus Streamlines Production of Allogeneic Gene-Edited CAR T Cells
Macleod, D.T. et al. Molecular Therapy. 4, 949-961 (2017).
Off the Shelf T Cell Therapies for Hematologic Malignancies
McCreedy, B. J. et al. Best Pract Res Clin Haematol. 2, 166-175 (2018).