OUR APPROACH | Gene Therapy

Gene therapies have the power to treat disease at the DNA level and address severe unmet medical needs.

At Precision BioSciences. we are focused on applying our proprietary ARCUS genome editing technology to cure genetic and infectious diseases where no adequate treatments exist. Gene editing technology has the incredible power to permanently cure devastating diseases; however, because gene edits are permanent, the risk of off-target or off-tissue gene edits can present a significant safety challenge.

Unlike some gene editing technologies that were designed primarily as research tools and subsequently engineered for therapeutic use, ARCUS was designed with therapeutic safety, delivery and control in mind. We believe our ARCUS platform has several significant advantages for use directly in vivo:

  • Highly specific ARCUS platform
  • Potential to treat a wide range of diseases
  • Ease of delivery

We have developed a robust pipeline of gene correction therapy candidates with a focus on diseases that have a clearly established genetic cause. To learn more about our lead programs, see our current corporate deck.